FDA Approves Leucovorin as First Drug for Rare Genetic Disorder
This approval follows previous claims of its potential use in treating autism symptoms.
Editorial Staff
1 min read
Updated 4 months ago
Updates
Update at 16:30 UTC on 2026-03-10
STAT reported The FDA approves leucovorin for a rare brain disorder while retreating from top officials’ earlier insistence that it could benefit many children with autism.
Sources: STAT
Update at 14:16 UTC on 2026-03-11
STAT reported The FDA's decision raises questions about the approval process and the implications for future drug evaluations.
Sources: STAT